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1994年9月初,研究人员报道了把囊性纤维化(CF)基因正常形式成功地转移到CF患者肺内壁细胞的消息。这是研究人员期望能矫正导致CF的基因缺陷的第一步。美国马里兰州贝塞斯达囊性纤维化基金会的Robert J Beall称,该结果对于证实基因转移用于治疗囊性纤维化的可行性是非常重要的。 1993年10月,依阿华大学的MichaelJWelsh报道了把正常CF基因插入3例囊性纤
In early September 1994, researchers reported the successful transfer of the normal form of the cystic fibrosis (CF) gene to the lung wall cells of CF patients. This is the first step researchers are looking to correct the genetic defects that cause CF. Robert J Beall of the Bethesda Cystic Fibrosis Foundation in Maryland, Maryland, said the results are important for demonstrating the feasibility of gene transfer for the treatment of cystic fibrosis. In October 1993, Michael Jewelsh of Iowa University reported that insertion of the normal CF gene into three cystic fibroids