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[会议论文] 作者:Karen Aiach, 来源:The 2nd International Rare Diseases Research Consortium Conf 年份:2014
Mucopolysaccharidosis type ⅢA (MPSⅢA),also known as Sanfilippo Syndrome type A,is a rare,autosomal recessive,lysosomal disease caused by mutations in N-sulfog...
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