Enzyme Replacement Therapy With Taliglucerase Alfa: 36-Month Safety and Efficacy Results in Adult Pa

来源 :The 35th World Congress of the International Society of Hema | 被引量 : 0次 | 上传用户：soloviola

【摘要】

：

【作者】

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Ari Zimran Suma P Shankar Milan Petakov Pilar Giraldo Hanna Rosenbaum Dominick J Amato Jeffrey Szer Raul Chertkoff Einat Brill-Almon Gregory M.Pastores

【机构】

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Department of Medicine/National Centre for Inherited Metabolic Disorders Mater Misericordiae Univers

【出处】

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The 35th World Congress of the International Society of Hema

【发表日期】

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2014年5期

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Objective Taliglucerase alfa is the first approved plant cell-expressed recombinant human protein and is an enzyme replacement therapy indicated for treatment of adults with Type 1 Gaucher disease (GD).In study PB-06-002,safety and efficacy were evaluated in 26 adult patients switched from imiglucerase to taliglucerase alfa.

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