Oligonucleotides such as siRNAs, antimiRs, miRNA mimics, IncRNAs and antisense oligonucleotides offer unique opportunities for developing novel therapeutic
Small molecule therapeutics are the well-established backbone of the pharmaceutical industrys contribution to public health, while monoclonal antibodies and
Eboia virus (EBOV) causes a highly lethal hemorrhagic fever syndrome in humans and has been associated with mortality rates of up to 91% in Zaire, the most
Eteplirsen induces skipping of exon 51 in dystrophin pre-mRNA in the muscles of DMD patients treated with the drug.This treatment restores the reading frame
On the basis of an in vitro evolutionary process, mirror-image RNA or DNA oligonucleotides can be identified to bind and inhibit pharmacologically relevant