近日,美国科学家通过基因疗法剔除了患有遗传性脑病实验鼠的不良基因,成功地控制了实验鼠病情的发展,该研究成果刊登在新一期英国《自然医学》杂志上。 研究人员采用RNA干扰技术,剔除患有脊髓小脑共济失调症病鼠脑细胞中的不良基因,使其脑细胞不再产生有毒蛋白质,进而停止对大脑的损伤。在接受治疗半年后,实验鼠的活动逐渐恢复正常,而未接受治疗的对照组实验鼠的病情进一 Recently, U.S. scientists succeeded in controlling the development of the experimental rat by excluding the bad genes from the mice with hereditary encephalopathy through gene therapy, and the research results are published in the new issue of the journal Nature Medicine. Researchers using RNA interference technology, excluding patients with spinocerebellar ataxia brain cells in the bad genes, so that brain cells no longer produce toxic proteins, and then stop the damage to the brain. After six months of treatment, the activity of the experimental mice gradually returned to normal, but the experimental mice in the untreated control group went one